Clinical Trial Update: PBA Use for Treatment of ATF6-/- Patients [EARLY_Phase 1]

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Summary

The EARLY Phase 1 clinical trial evaluating phenylbutyrate for ATF6-/- patients with achromatopsia is currently suspended, in a study sponsored by Columbia Univ…

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Diseases / indications

• Achromatopsia

Drugs mentioned

• Phenylbutyrate (phenylbutyrate)

Snippet

Sponsor: Columbia University | Conditions: ACHROMATOPSIA 7, Achromatopsia | EARLY_Phase 1 | Status: SUSPENDED