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CLINICAL_TRIALS trial_result · 2025-09-17

Clinical Trial Update: Effects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD) [Phase 3]

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Summary

Phase 3 clinical trial evaluating miglustat therapy for infantile GM2 gangliosidosis (Sandhoff and Tay-Sachs diseases) has been terminated.

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Diseases / indications

Drugs mentioned

  • Miglustat (miglustat)

Snippet

Sponsor: Tehran University of Medical Sciences | Conditions: GM2 Gangliosidosis, Supportive Care | Phase 3 | Status: TERMINATED