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CLINICAL_TRIALS research · 2025-09-23

Clinical Trial Update: (PIONEER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, Versus Placebo in Patients With Indolent Systemic Mastocytosis [Phase 2]

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Summary

The document outlines a Phase 2 clinical trial, PIONEER, evaluating the efficacy and safety of avapritinib versus placebo in patients with indolent systemic mas…

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Diseases / indications

Drugs mentioned

  • Avapritinib (BLU-285) (avapritinib)

Snippet

Sponsor: Blueprint Medicines Corporation | Conditions: Indolent Systemic Mastocytosis | Phase 2 | Status: ACTIVE_NOT_RECRUITING