CLINICAL_TRIALS
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· 2025-09-23
Clinical Trial Update: (PIONEER) Study to Evaluate Efficacy and Safety of Avapritinib (BLU-285), A Selective KIT Mutation-targeted Tyrosine Kinase Inhibitor, Versus Placebo in Patients With Indolent Systemic Mastocytosis [Phase 2]
Summary
The document outlines a Phase 2 clinical trial, PIONEER, evaluating the efficacy and safety of avapritinib versus placebo in patients with indolent systemic mas…
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Snippet
Sponsor: Blueprint Medicines Corporation | Conditions: Indolent Systemic Mastocytosis | Phase 2 | Status: ACTIVE_NOT_RECRUITING