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CLINICAL_TRIALS trial_result · 2025-09-25

Clinical Trial Update: Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG [Phase 3]

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Summary

A Phase 3 trial evaluating oral epalrestat in pediatric subjects with PMM2-CDG has been terminated.

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Diseases / indications

Drugs mentioned

  • epalrestat (epalrestat)

Snippet

Sponsor: Maggie's Pearl, LLC | Conditions: Pmm2-CDG, Phosphomannomutase 2 Deficiency | Phase 3 | Status: TERMINATED