Clinical Trial Update: Acute Rhabdomyolysis and Muscle Pain Associated With Mutations in the LPIN1 Gene - A Retrospective Study Describing the Safety and Efficacy of Hydroxychloroquine Sulfate Given on a Compassionate Basis to Patients Suffering From Lipin-1 Deficiency

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Summary

A retrospective study evaluated compassionate-use hydroxychloroquine sulfate in patients with Lipin-1 deficiency, focusing on safety and rhabdomyolysis-related …

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Diseases / indications

• Lipin-1 Deficiency

Drugs mentioned

• Hydroxychloroquine sulfate (Hydroxychloroquine sulfate)

Snippet

Sponsor: Assistance Publique - Hôpitaux de Paris | Conditions: LIPIN1 Deficiency | Status: WITHDRAWN