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CLINICAL_TRIALS trial_result · 2025-09-26

Clinical Trial Update: Study for Adolescents and Adults With Ornithine Transcarbamylase Deficiency to Evaluate Safety and Tolerability of ARCT-810 [Phase 2]

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Summary

A Phase 2 study evaluating ARCT-810 for Ornithine transcarbamylase deficiency has been terminated, representing a status update on the trial in adolescents and …

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Diseases / indications

Drugs mentioned

  • ARCT-810

Snippet

Sponsor: Arcturus Therapeutics, Inc. | Conditions: Ornithine Transcarbamylase Deficiency, OTC Deficiency | Phase 2 | Status: TERMINATED