CLINICAL_TRIALS
trial_result
· 2025-09-26
Clinical Trial Update: Study of Sodium Phenylbutyrate (ACER-001) for the Treatment of Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD) [Phase 2]
Summary
A Phase 2 clinical trial evaluating ACER-001 (sodium phenylbutyrate) for Medium-chain Acyl-CoA Dehydrogenase Deficiency has been suspended.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Jerry Vockley, MD, PhD | Conditions: Medium-chain Acyl-CoA Dehydrogenase Deficiency | Phase 2 | Status: SUSPENDED