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CLINICAL_TRIALS research · 2025-09-29

Clinical Trial Update: HBCMD01- Expanded Access for the Treatment of Congenital Muscular Dystrophy.

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Summary

Expanded access program HBCMD01 for congenital muscular dystrophy due to LMNA mutation is no longer available.

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Diseases / indications

Drugs mentioned

  • HBCMD01

Snippet

Sponsor: Hope Biosciences Research Foundation | Conditions: Congenital Muscular Dystrophy Due to Lamin A/C Mutation | Status: NO_LONGER_AVAILABLE