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CLINICAL_TRIALS research · 2025-09-29

Clinical Trial Update: A Clinical Study to Evaluate the Use of a Cryopreserved Formulation of OTL-103 in Subjects With Wiskott-Aldrich Syndrome [Phase 3]

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Summary

Phase 3 clinical trial evaluating a cryopreserved formulation of OTL-103 for Wiskott-Aldrich Syndrome. The study is currently active but not recruiting.

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Diseases / indications

Drugs mentioned

  • OTL-103

Snippet

Sponsor: Fondazione Telethon | Conditions: Wiskott-Aldrich Syndrome | Phase 3 | Status: ACTIVE_NOT_RECRUITING