CLINICAL_TRIALS
trial_result
· 2025-10-03
Clinical Trial Update: Long-term Follow-up (LTFU) of Patients Treated With Genome-edited Autologous Hematopoietic Stem and Progenitor Cells (HSPC) [Phase 1]
Summary
This clinical trial update provides long-term follow-up results for sickle cell disease patients treated with genome-edited autologous hematopoietic stem and pr…
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Novartis Pharmaceuticals | Conditions: Sickle Cell Disease | Phase 1 | Status: ACTIVE_NOT_RECRUITING