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CLINICAL_TRIALS trial_result · 2025-10-03

Clinical Trial Update: Long-term Follow-up (LTFU) of Patients Treated With Genome-edited Autologous Hematopoietic Stem and Progenitor Cells (HSPC) [Phase 1]

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Summary

This clinical trial update provides long-term follow-up results for sickle cell disease patients treated with genome-edited autologous hematopoietic stem and pr…

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Diseases / indications

Drugs mentioned

  • Genome-edited autologous hematopoietic stem and progenitor cells (HSPCs)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Sickle Cell Disease | Phase 1 | Status: ACTIVE_NOT_RECRUITING