Clinical Trial Update: A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease [Phase 2]

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Summary

This is a Phase 2 clinical trial update for RP-A501 in male patients with Danon disease, with recruitment currently ongoing.

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Diseases / indications

• Danon Disease

Drugs mentioned

• RP-A501

Snippet

Sponsor: Rocket Pharmaceuticals Inc. | Conditions: Danon Disease | Phase 2 | Status: RECRUITING