Clinical Trial Update: Long-Term Follow-Up of Subjects Treated With AXO-AAV-GM2 for Tay-Sachs or Sandhoff Disease

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Summary

This clinical trial update reports long-term follow-up data for subjects treated with AXO-AAV-GM2 in GM2 gangliosidosis (Tay-Sachs and Sandhoff diseases), descr…

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Diseases / indications

• Gm2 Gangliosidosis
• Sandhoff Disease
• Tay-sachs Disease

Drugs mentioned

• AXO-AAV-GM2

Snippet

Sponsor: Terence Flotte | Conditions: GM2 Gangliosidosis, Tay Sachs Disease | Status: ACTIVE_NOT_RECRUITING