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CLINICAL_TRIALS trial_result · 2024-10-28

Clinical Trial Update: Study to Evaluate Patients With Cerebrotendinous Xanthomatosis (RESTORE) [Phase 3]

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Summary

A Phase 3 RESTORE trial evaluating a Mirum Pharmaceuticals therapy for Cerebrotendinous Xanthomatosis has completed, with results posted.

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Diseases / indications

Snippet

Sponsor: Mirum Pharmaceuticals, Inc. | Conditions: CTX | Phase 3 | Status: COMPLETED | Results posted: 2024-10-28