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CLINICAL_TRIALS trial_result · 2024-10-30

Clinical Trial Update: Long Term Follow Up Of Patients Who Have Received Gene Therapy Or Gene Marked Products

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Summary

Long-term follow-up results are reported for patients who received gene therapy or gene-marked products across several conditions, including SCID and mucopolysa…

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Diseases / indications

Snippet

Sponsor: St. Jude Children's Research Hospital | Conditions: Severe Combined Immunodeficiency, Malignancy, Hematologic | Status: COMPLETED