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CLINICAL_TRIALS research · 2024-11-20

Clinical Trial Update: Spinraza in Adult Spinal Muscular Atrophy

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Summary

Clinical trial update showing Spinraza (nusinersen) being studied in adults with Spinal Muscular Atrophy, including SMA Type II and SMA Type III, with the study…

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Diseases / indications

Drugs mentioned

  • Spinraza (nusinersen)

Snippet

Sponsor: Washington University School of Medicine | Conditions: Spinal Muscular Atrophy, Spinal Muscular Atrophy Type II | Status: ACTIVE_NOT_RECRUITING