Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2024-11-22

Clinical Trial Update: Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)

View source ↗

Summary

A natural history study of homocystinuria caused by cystathionine beta-synthase deficiency is currently recruiting.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Snippet

Sponsor: Travere Therapeutics, Inc. | Conditions: Homocystinuria Due to CBS Deficiency | Status: RECRUITING