CLINICAL_TRIALS
research
· 2024-11-22
Clinical Trial Update: Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)
Summary
A natural history study of homocystinuria caused by cystathionine beta-synthase deficiency is currently recruiting.
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Diseases / indications
Snippet
Sponsor: Travere Therapeutics, Inc. | Conditions: Homocystinuria Due to CBS Deficiency | Status: RECRUITING