Clinical Trial Update: Pegtibatinase As an Enzyme Therapy for Patients with Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (COMPOSE) [Phase 1, Phase 2]

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Summary

Pegtibatinase is being studied in a Phase 1/Phase 2 trial for homocystinuria caused by cystathionine beta-synthase deficiency, sponsored by Travere Therapeutics…

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Diseases / indications

• Homocystinuria

Drugs mentioned

• Pegtibatinase (pegtibatinase)

Snippet

Sponsor: Travere Therapeutics, Inc. | Conditions: Homocystinuria | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING