EMA Authorised: Zolgensma (onasemnogene abeparvovec) — Novartis Europharm Limited

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Summary

EMA authorised Zolgensma (onasemnogene abeparvovec) for spinal muscular atrophy under conditional approval and orphan designation.

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Diseases / indications

• Spinal Muscular Atrophy

Drugs mentioned

• Zolgensma (onasemnogene abeparvovec)

Snippet

Status: Authorised. Therapeutic area: Muscular Atrophy, Spinal. MAH: Novartis Europharm Limited. Decision date: 23/06/2026. Conditional approval. Orphan medicine