Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2026-06-25

Clinical Trial Results: Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of SAR442501 in Pediatric Participants With Achondroplasia [Phase 2]

View source ↗

Summary

Phase 2 trial results for SAR442501 in pediatric achondroplasia (osteochondrodysplasia) assessing safety, tolerability, PK/PD, and efficacy; study terminated wi…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • SAR442501

Snippet

Sponsor: Sanofi | Conditions: Osteochondrodysplasia | Phase 2 | Status: TERMINATED | Results posted: 2026-06-25