Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2026-06-23

Clinical Trial Update: A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria [Phase 3]

View source ↗

Summary

Long-term safety study update for PTC923 in participants with Phenylketonuria (Phase 3).

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • PTC923

Snippet

Sponsor: PTC Therapeutics | Conditions: Phenylketonuria | Phase 3 | Status: ACTIVE_NOT_RECRUITING