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CLINICAL_TRIALS research · 2026-06-05

Clinical Trial Update: Pegcetacoplan Long Term Safety and Efficacy Extension Study [Phase 3]

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Summary

Phase 3 long-term safety and efficacy extension study for pegcetacoplan in paroxysmal nocturnal hemoglobinuria (PNH) completed.

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Diseases / indications

Drugs mentioned

  • Pegcetacoplan (Pegcetacoplan)

Snippet

Sponsor: Apellis Pharmaceuticals, Inc. | Conditions: PNH | Phase 3 | Status: COMPLETED