FDA Approves First Treatment for Patients with Cerebral Folate Transport Deficiency

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Summary

FDA approves expanded use of Wellcovorin (leucovorin calcium) to treat cerebral folate deficiency in patients with CFD-FOLR1.

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Diseases / indications

• Cerebral Folate Deficiency

Drugs mentioned

• Wellcovorin (leucovorin calcium)

Snippet

The U.S. Food and Drug Administration today approved expanded use of Wellcovorin (leucovorin calcium) tablets for the treatment of cerebral folate deficiency in adult and pediatric patients who have a confirmed variant in the folate receptor 1 gene (CFD-FOLR1).