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CLINICAL_TRIALS research · 2024-12-12

Clinical Trial Update: Natural History Study of Children With LAMA2-related Dystrophies

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Summary

A natural history study protocol for children with LAMA2-related dystrophies (Merosin-deficient congenital muscular dystrophy) is currently recruiting, sponsore…

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Diseases / indications

Snippet

Sponsor: Institut de Myologie, France | Conditions: Merosin Deficient Congenital Muscular Dystrophy | Status: RECRUITING