CLINICAL_TRIALS
trial_result
· 2024-02-07
Clinical Trial Update: Risdiplam in Patients With Spinal Muscular Atrophy Previously Treated With Nusinersen [Phase 4]
Summary
Phase 4 trial update evaluating risdiplam in patients with spinal muscular atrophy previously treated with nusinersen.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Clinic for Special Children | Conditions: Spinal Muscular Atrophy | Phase 4 | Status: ACTIVE_NOT_RECRUITING