Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2024-02-07

Clinical Trial Update: Risdiplam in Patients With Spinal Muscular Atrophy Previously Treated With Nusinersen [Phase 4]

View source ↗

Summary

Phase 4 trial update evaluating risdiplam in patients with spinal muscular atrophy previously treated with nusinersen.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • Risdiplam (risdiplam)

Snippet

Sponsor: Clinic for Special Children | Conditions: Spinal Muscular Atrophy | Phase 4 | Status: ACTIVE_NOT_RECRUITING