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CLINICAL_TRIALS trial_result · 2024-02-20

Clinical Trial Update: Study of Subretinally Injected ATSN-101 Administered in Patients With Leber Congenital Amaurosis Caused by Biallelic Mutations in GUCY2D [Phase 1, Phase 2]

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Summary

A phase 1/2 clinical trial evaluating subretinal ATSN-101 for Leber congenital amaurosis caused by biallelic GUCY2D mutations is currently active but not recrui…

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Diseases / indications

Drugs mentioned

  • ATSN-101

Snippet

Sponsor: Atsena Therapeutics Inc. | Conditions: Leber Congenital Amaurosis, LCA | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING