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CLINICAL_TRIALS trial_result · 2024-02-23

Clinical Trial Update: Gene Therapy With hLB-001 in Pediatric Patients With Severe Methylmalonic Acidemia [Phase 1, Phase 2]

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Summary

A Phase 1/2 clinical trial of gene therapy hLB-001 in pediatric patients with methylmalonic acidemia has terminated with results posted.

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Diseases / indications

Drugs mentioned

  • hLB-001

Snippet

Sponsor: LogicBio Therapeutics, Inc | Conditions: Methylmalonic Acidemia | Phase 1, Phase 2 | Status: TERMINATED | Results posted: 2024-02-23