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CLINICAL_TRIALS research · 2024-12-19

Clinical Trial Update: Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases

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Summary

A clinical trial update reports completion of a genetics study on pediatric-onset motor neuron and neuromuscular diseases, including spinal muscular atrophy and…

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Diseases / indications

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Sponsor: Nemours Children's Clinic | Conditions: Spinal Muscular Atrophy, Charcot-Marie-Tooth Disease | Status: COMPLETED