Clinical Trial Update: Evaluating Safety and Efficacy of Autologous Gene-edited Muscle Stem Cells (GenPHSats-bASKet) [Phase 1, Phase 2]

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Summary

A clinical trial update describes evaluating safety and efficacy of autologous gene-edited muscle stem cells (GenPHSats-bASKet) in limb girdle muscular dystroph…

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Diseases / indications

• Limb Girdle Muscular Dystrophy

Drugs mentioned

• GenPHSats-bASKet

Snippet

Sponsor: Simone Spuler, MD | Conditions: LGMD | Phase 1, Phase 2 | Status: UNKNOWN