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CLINICAL_TRIALS trial_result · 2023-09-22

Clinical Trial Update: A Second-generation AI Based Therapeutic Regimen in Patients With Gaucher Disease Treated With Enzyme Replacement Therapy. [Phase 2]

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Summary

A Phase 2 clinical trial reports on a second-generation AI-based therapeutic regimen for Gaucher disease type 1 in patients already treated with enzyme replacem…

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Diseases / indications

Drugs mentioned

  • Enzyme Replacement Therapy (enzyme replacement therapy)
  • Second-generation AI-based therapeutic regimen

Snippet

Sponsor: Hadassah Medical Organization | Conditions: Gaucher Disease Type 1 | Phase 2 | Status: COMPLETED