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CLINICAL_TRIALS trial_result · 2025-01-03

Clinical Trial Update: BCX9930 for the Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH) in Participants Not Receiving Other Complement Inhibitor Therapy [Phase 2]

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Summary

A Phase 2 trial evaluating BCX9930 for Paroxysmal Nocturnal Hemoglobinuria in participants not receiving other complement inhibitors was terminated, with result…

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Diseases / indications

Drugs mentioned

  • BCX9930 (Factor D inhibitor)

Snippet

Sponsor: BioCryst Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria (PNH) | Phase 2 | Status: TERMINATED | Results posted: 2025-01-03