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CLINICAL_TRIALS trial_result · 2023-11-02

Clinical Trial Update: A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of Multiple Subcutaneous Doses of TransCon CNP Administered Once Weekly in Children With Achondroplasia [Phase 2]

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Summary

A Phase 2 dose-escalation trial is evaluating safety, efficacy, and pharmacokinetics of weekly subcutaneous TransCon CNP in children with Achondroplasia.

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Diseases / indications

Drugs mentioned

  • TransCon CNP (C-type natriuretic peptide prodrug)

Snippet

Sponsor: Ascendis Pharma A/S | Conditions: Achondroplasia | Phase 2 | Status: UNKNOWN