CLINICAL_TRIALS
trial_result
· 2025-01-08
Clinical Trial Update: Dose Escalation of BCX10013 in Participants with Paroxysmal Nocturnal Hemoglobinuria (PNH) [Phase 1]
Summary
This Phase 1 dose-escalation trial of BCX10013 in Paroxysmal nocturnal hemoglobinuria has completed its dose-escalation portion.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: BioCryst Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Phase 1 | Status: COMPLETED