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CLINICAL_TRIALS trial_result · 2025-01-08

Clinical Trial Update: Dose Escalation of BCX10013 in Participants with Paroxysmal Nocturnal Hemoglobinuria (PNH) [Phase 1]

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Summary

This Phase 1 dose-escalation trial of BCX10013 in Paroxysmal nocturnal hemoglobinuria has completed its dose-escalation portion.

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Diseases / indications

Drugs mentioned

  • BCX10013

Snippet

Sponsor: BioCryst Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Phase 1 | Status: COMPLETED