Clinical Trial Update: Open-label Study of VTS-270 in Participants With Neurologic Manifestations of Niemann-Pick Type C1 [Phase 2, Phase 3]

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Summary

Open-label study of VTS-270 in neurologic manifestations of Niemann-Pick disease type C1 was terminated; results have been posted.

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Diseases / indications

• Niemann-pick Disease Type

Drugs mentioned

• VTS-270 (2-hydroxypropyl-beta-cyclodextrin)

Snippet

Sponsor: Mandos LLC | Conditions: Niemann-Pick Disease, Type C | Phase 2, Phase 3 | Status: TERMINATED | Results posted: 2023-12-26