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CLINICAL_TRIALS trial_result · 2025-01-15

Clinical Trial Update: A Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With Zolgensma

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Summary

A long-term safety study in Brazilian patients with spinal muscular atrophy treated with Zolgensma is currently recruiting.

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Diseases / indications

Drugs mentioned

  • Zolgensma (onasemnogene abeparvovec)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Spinal Muscular Atrophies | Status: RECRUITING