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CLINICAL_TRIALS ClinicalTrials.gov record update

Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders

This page presents selected fields from the linked source record. It does not add a medical interpretation.

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT01372228
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-28T10:39:13.662706+00:00
Published At
2023-04-12T00:00:00+00:00
Record Updated At
2023-04-12
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Hurler Syndrome (MPS I)", "Hurler-Scheie Syndrome", "Hunter Syndrome (MPS II)", "Sanfilippo Syndrome (MPS III)", "Krabbe Disease (Globoid Leukodystrophy)", "Metachromatic Leukodystrophy (MLD)", "Adrenoleukodystrophy (ALD and AMN)", "Sandhoff Disease", "Tay Sachs Disease", "Pelizaeus Merzbacher (PMD)", "Niemann-Pick Disease", "Alpha-mannosidosis"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2023-04-12"
protocolSection.identificationModule.nctId
"NCT01372228"
protocolSection.identificationModule.officialTitle
"Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders"
protocolSection.statusModule.overallStatus
"TERMINATED"
protocolSection.designModule.phases
["PHASE1", "PHASE2"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • Hurler Syndrome (MPS I) (protocolSection.conditionsModule.conditions)
  • Hurler-Scheie Syndrome (protocolSection.conditionsModule.conditions)
  • Hunter Syndrome (MPS II) (protocolSection.conditionsModule.conditions)
  • Sanfilippo Syndrome (MPS III) (protocolSection.conditionsModule.conditions)
  • Krabbe Disease (Globoid Leukodystrophy) (protocolSection.conditionsModule.conditions)
  • Metachromatic Leukodystrophy (MLD) (protocolSection.conditionsModule.conditions)
  • Adrenoleukodystrophy (ALD and AMN) (protocolSection.conditionsModule.conditions)
  • Sandhoff Disease (protocolSection.conditionsModule.conditions)
  • Tay Sachs Disease (protocolSection.conditionsModule.conditions)
  • Pelizaeus Merzbacher (PMD) (protocolSection.conditionsModule.conditions)
  • Niemann-Pick Disease (protocolSection.conditionsModule.conditions)
  • Alpha-mannosidosis (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

This index keeps the source fields it imported; it may not contain the complete original record. Verify wording and context in the linked source.