Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2025-01-27

Clinical Trial Update: In Utero Hematopoietic Stem Cell Transplantation for Alpha-thalassemia Major (ATM) [Phase 1]

View source ↗

Summary

Phase 1 in utero hematopoietic stem cell transplantation for Alpha-thalassemia major has been terminated.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Snippet

Sponsor: University of California, San Francisco | Conditions: Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia | Phase 1 | Status: TERMINATED