CLINICAL_TRIALS
trial_result
· 2025-01-27
Clinical Trial Update: In Utero Hematopoietic Stem Cell Transplantation for Alpha-thalassemia Major (ATM) [Phase 1]
Summary
Phase 1 in utero hematopoietic stem cell transplantation for Alpha-thalassemia major has been terminated.
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Diseases / indications
Snippet
Sponsor: University of California, San Francisco | Conditions: Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia | Phase 1 | Status: TERMINATED