Clinical Trial Update: Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia [Phase 1, Phase 2]

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Summary

Pilot Phase I/II study evaluating amino acid leucine for transfusion-dependent Diamond Blackfan Anemia has completed with results posted.

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Diseases / indications

• Diamond-blackfan Anemia

Drugs mentioned

• Amino acid leucine (leucine)

Snippet

Sponsor: Northwell Health | Conditions: Diamond Blackfan Anemia, Blackfan Diamond Syndrome | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2022-12-02