Clinical Trial Update: A Natural History Study of Biomarkers and Clinical Outcomes in Mucopolysaccharidosis Type IIIA (MPS IIIA; Sanfilippo Syndrome)

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Summary

This ClinicalTrials.gov update notes the completion of a natural history study evaluating biomarkers and clinical outcomes in Mucopolysaccharidosis type IIIA (S…

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Diseases / indications

• Mucopolysaccharidosis Type Iiia
• Sanfilippo Syndrome Type

Snippet

Sponsor: Sanguine Biosciences | Conditions: Mucopolysaccharidosis III-A | Status: COMPLETED