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CLINICAL_TRIALS trial_result · 2025-01-31

Clinical Trial Update: An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome [Phase 2]

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Summary

This update notes the completion of a Phase 2 open-label study evaluating the safety, tolerability, and pharmacokinetics of oral NNZ-2591 in Angelman syndrome.

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Diseases / indications

Drugs mentioned

  • NNZ-2591 (NNZ-2591)

Snippet

Sponsor: Neuren Pharmaceuticals Limited | Conditions: Angelman Syndrome | Phase 2 | Status: COMPLETED