CLINICAL_TRIALS ClinicalTrials.gov record update

An Open-Label, Dose Escalation and Double-Masked, Randomized, Controlled Study to Evaluate the Safety and Tolerability of Sepofarsen in Pediatric Subjects <8 Years of Age With Leber Congenital Amaurosis Type 10 (LCA10) Due to the c.2991 +1655A>G (p.Cys998X) Mutation.

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Record identity and dates

Source: ClinicalTrials.gov
Source record ID: NCT04855045
Title field or adapter rule: protocolSection.identificationModule.officialTitle
Ingested At: 2026-04-28T10:38:44.676935+00:00
Published At: 2022-03-25T00:00:00+00:00
Record Updated At: 2022-03-25
Timestamp Basis: source retrieval time was not retained by the feed adapter
Date limitation: source retrieval time was not retained by the feed adapter

protocolSection.conditionsModule.conditions: ["Leber Congenital Amaurosis 10", "Blindness", "Leber Congenital Amaurosis", "Vision Disorders", "Sensation Disorders", "Neurologic Manifestations", "Eye Diseases", "Eye Disorders Congenital", "Retinal Disease", "Retinal Degeneration", "Retinal Dystrophies"]
protocolSection.statusModule.lastUpdatePostDateStruct.date: "2022-03-25"
protocolSection.identificationModule.nctId: "NCT04855045"
protocolSection.identificationModule.officialTitle: "An Open-Label, Dose Escalation and Double-Masked, Randomized, Controlled Study to Evaluate the Safety and Tolerability of Sepofarsen in Pediatric Subjects \u003c8 Years of Age With Leber Congenital Amaurosis Type 10 (LCA10) Due to the c.2991 +1655A\u003eG (p.Cys998X) Mutation."
protocolSection.statusModule.overallStatus: "UNKNOWN"
protocolSection.designModule.phases: ["PHASE2", "PHASE3"]
protocolSection.statusModule.resultsFirstPostDateStruct.date: ""

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