CLINICAL_TRIALS
trial_result
· 2025-02-04
Clinical Trial Update: Miglustat in Niemann-Pick Type C Disease [Phase 2]
Summary
Phase 2 trial of miglustat for Niemann-Pick disease type C has completed.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Actelion | Conditions: Niemann-Pick Type C Disease | Phase 2 | Status: COMPLETED