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CLINICAL_TRIALS trial_result · 2025-02-04

Clinical Trial Update: Miglustat in Niemann-Pick Type C Disease [Phase 2]

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Summary

Phase 2 trial of miglustat for Niemann-Pick disease type C has completed.

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Diseases / indications

Drugs mentioned

  • Zavesca (Miglustat)

Snippet

Sponsor: Actelion | Conditions: Niemann-Pick Type C Disease | Phase 2 | Status: COMPLETED