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CLINICAL_TRIALS trial_result · 2025-02-06

Clinical Trial Update: Data Analysis of Adult and Pediatric Participants With Acid Sphingomyelinase Deficiency (ASMD) on Early Access to Olipudase Alfa in France

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Summary

This document reports a completed data analysis of adult and pediatric participants with acid sphingomyelinase deficiency (ASMD) who received early access to ol…

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Diseases / indications

Drugs mentioned

  • Xenpozyme (olipudase alfa) (olipudase alfa)

Snippet

Sponsor: Sanofi | Conditions: Acid Sphingomyelinase Deficiency (ASMD) | Status: COMPLETED