CLINICAL_TRIALS
trial_result
· 2025-02-06
Clinical Trial Update: Data Analysis of Adult and Pediatric Participants With Acid Sphingomyelinase Deficiency (ASMD) on Early Access to Olipudase Alfa in France
Summary
This document reports a completed data analysis of adult and pediatric participants with acid sphingomyelinase deficiency (ASMD) who received early access to ol…
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Sanofi | Conditions: Acid Sphingomyelinase Deficiency (ASMD) | Status: COMPLETED