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CLINICAL_TRIALS trial_result · 2022-05-24

Clinical Trial Update: A Study to Evaluate Efficacy and Safety of AG-348 in Not Regularly Transfused Adult Participants With Pyruvate Kinase Deficiency (PKD) [Phase 3]

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Summary

Phase 3 trial evaluating AG-348 (mitapivat) for efficacy and safety in not regularly transfused adults with pyruvate kinase deficiency has completed with result…

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Diseases / indications

Drugs mentioned

  • AG-348 (mitapivat)

Snippet

Sponsor: Agios Pharmaceuticals, Inc. | Conditions: Pyruvate Kinase Deficiency, Anemia, Hemolytic | Phase 3 | Status: COMPLETED | Results posted: 2022-05-24