Clinical Trial Update: Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy [Phase 1, Phase 2]

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Summary

Clinical trial update for autologous hematopoietic stem cell gene therapy targeting Metachromatic Leukodystrophy and Adrenoleukodystrophy in Phase 1/2.

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Diseases / indications

• Adrenoleukodystrophy
• Metachromatic Leukodystrophy

Snippet

Sponsor: Shenzhen Second People's Hospital | Conditions: Metachromatic Leukodystrophy, Adrenoleukodystrophy | Phase 1, Phase 2 | Status: UNKNOWN