CLINICAL_TRIALS
trial_result
· 2022-07-22
Clinical Trial Update: Safety and Efficacy Trial of AAV Gene Therapy in Patients With CNGB3 Achromatopsia (A Clarity Clinical Trial) [Phase 1, Phase 2]
Summary
Aacygene therapy trial (AAV) for CNGB3-related achromatopsia is ongoing in Phase 1/2 to assess safety and efficacy.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Beacon Therapeutics | Conditions: Achromatopsia | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING