Clinical Trial Update: Study of AAVrh10-h.SGSH Gene Therapy in Patients With Mucopolysaccharidosis Type IIIA (MPS IIIA) [Phase 2, Phase 3]

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Summary

A study of AAVrh10-h.SGSH gene therapy in MPS IIIA is in Phase 2/3 with status not provided.

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Diseases / indications

• Mucopolysaccharidosis Type Iiia

Drugs mentioned

• AAVrh10-h.SGSH gene therapy (AAVrh10-h.SGSH)

Snippet

Sponsor: LYSOGENE | Conditions: Mucopolysaccharidosis Type IIIA | Phase 2, Phase 3 | Status: UNKNOWN