Clinical Trial Update: Use of Phenylbutyrate Therapy for Patients With Pyruvate Dehydrogenase Complex Deficiency. [Phase 2]

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Summary

A Phase 2 clinical trial evaluating phenylbutyrate therapy in patients with Pyruvate Dehydrogenase Complex Deficiency has completed.

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Diseases / indications

• Pyruvate Dehydrogenase Complex Deficiency

Drugs mentioned

• Phenylbutyrate (phenylbutyrate)

Snippet

Sponsor: Fondazione Telethon | Conditions: Pyruvate Dehydrogenase Complex Deficiency | Phase 2 | Status: COMPLETED