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CLINICAL_TRIALS ClinicalTrials.gov record update

Natural History Study for Pediatric Patients With Early Onset of Either GM1 Gangliosidosis, GM2 Gangliosidoses, or Gaucher Disease Type 2

This page presents selected fields from the linked source record. It does not add a medical interpretation.

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT04470713
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-28T10:38:24.673250+00:00
Published At
2021-11-08T00:00:00+00:00
Record Updated At
2021-11-08
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["GM1 Gangliosidosis", "GM2 Gangliosidosis", "Gaucher Disease, Type 2", "Tay-Sachs Disease", "AB Variant Gangliosidosis GM2", "Sandhoff Disease"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2021-11-08"
protocolSection.identificationModule.nctId
"NCT04470713"
protocolSection.identificationModule.officialTitle
"Natural History Study for Pediatric Patients With Early Onset of Either GM1 Gangliosidosis, GM2 Gangliosidoses, or Gaucher Disease Type 2"
protocolSection.statusModule.overallStatus
"COMPLETED"
protocolSection.designModule.phases
[]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • GM1 Gangliosidosis (protocolSection.conditionsModule.conditions)
  • GM2 Gangliosidosis (protocolSection.conditionsModule.conditions)
  • Gaucher Disease, Type 2 (protocolSection.conditionsModule.conditions)
  • Tay-Sachs Disease (protocolSection.conditionsModule.conditions)
  • AB Variant Gangliosidosis GM2 (protocolSection.conditionsModule.conditions)
  • Sandhoff Disease (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

This index keeps the source fields it imported; it may not contain the complete original record. Verify wording and context in the linked source.