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CLINICAL_TRIALS trial_result · 2021-11-12

Clinical Trial Update: Testing SIROLIMUS in Beta-thalassemia Transfusion Dependent Patients (THALA-RAP) [Phase 2]

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Summary

Phase 2 clinical trial update investigating sirolimus for beta-thalassemia in transfusion-dependent patients.

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Diseases / indications

Drugs mentioned

  • Sirolimus (Sirolimus)

Snippet

Sponsor: Università degli Studi di Ferrara | Conditions: Beta-Thalassemia | Phase 2 | Status: UNKNOWN