Clinical Trial Update: A Study to Assess the Safety and Tolerability of SOBI003 in Pediatric MPS IIIA Patients [Phase 1, Phase 2]

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Summary

A clinical trial assessing safety and tolerability of SOBI003 in pediatric patients with Sanfilippo Syndrome Type A (MPS IIIA) has completed Phase 1/Phase 2 wit…

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Diseases / indications

• Mucopolysaccharidosis Type Iiia
• Sanfilippo Syndrome Type

Drugs mentioned

• SOBI003

Snippet

Sponsor: Swedish Orphan Biovitrum | Conditions: Sanfilippo Syndrome Type A (MPS IIIA) | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2021-04-22